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What is

Patisiran

?

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Pronunciation: /patisiran*/

Patisiran

Definition

(Other name for: anti-transthyretin siRNA ALN-TTR02)

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sclerotherapy

stereotactic procedure

chronic leukemia

troxacitabine

influenza A virus

genomic sequencing

alanine aminopeptidase

nephrectomy

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imsidolimab

TNFerade

allogeneic anti-CD19 CAR-NK cells QN-019a

Dymelor

soluble guanylate cyclase stimulator IW-1701

WT1 protein-derived peptide vaccine DSP-7888

balixafortide

autologous anti-GPC3 CAR T lymphocytes JWAT204

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presymptomatic testing

trichilemmoma

kindred

polymorphism

novel variant

consanguinity

loss of heterozygosity

somatic variant

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